Search results
FDA expands approval of first gene therapy for rare form of muscular dystrophy
WTAE Pittsburgh· 19 hours agoThe U.S. Food and Drug Administration has given the green light for the first gene therapy that...
Research paying off for Madison company
Wisconsin State Journal· 2 hours agoThirty years ago, when the idea that would give rise to Mirus Bio took shape in a UW-Madison laboratory, scientists were only beginning to piece together...
Gene therapy may cure rare diseases. But drugmakers have few incentives, leaving families desperate...
Texarkana Gazette· 7 hours agoRobin Alderman faces an agonizing reality: Gene therapy might cure her son Camden's rare, inherited...
Another Study Finds CRISPR Gene Therapy Fights Sickle Cell | FOX 28 Spokane
FOX 28 Spokane· 5 days ago“It’s encouraging that this gene-editing treatment continues to show promising efficacy for sickle...
Top FDA official overrules staff to approve gene therapy that failed trial
Ars Technica· 2 days agoThe Food and Drug Administration (FDA) on Thursday announced expanded approval for a gene therapy to...
Groundbreaking cancer treatment may trigger more cancer – but here’s why you shouldn’t worry
The Conversation· 3 days agoIn the last few decades, scientists have finally learned to harness the immune system to successfully treat cancer. Car-T therapy, short for “chimeric antigen receptor T-cell ...
Sarepta Catapults 30% After Hitting A 'Grand Slam' Approval
Investor's Business Daily· 2 days agoThe gene therapy, dubbed Elevidys, already had accelerated approval for children age 4 and 5 with the muscle-wasting disease. Late Thursday, the Food and ...
Global Nonprofit CureDuchenne to Host Informational Webinars Following FDA Label Expansion of...
The Yuma Sun· 2 days agoThe webinars will be moderated by Dr. Michael Kelly, Chief Scientific Officer at CureDuchenne with Dr. Diana Castro, a board-certified neurologist and leading neuromuscular physician, sharing ...
Low-income Floridians with sickle cell disease will have access to new gene therapies
Florida Phoenix via Yahoo News· 7 days agoNow, Floridians with sickle cell disease are closer to a functional cure after health care officials...
Dr. Phil's staged interview with Donald Trump is a sign of the grim political theater to come
Salon via Yahoo News· 2 days agoHe rose to popularity because of his appearances on "The Oprah Winfrey Show" where he offered a...