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Takeaways from AP's report on access to gene therapies for rare diseases
ABC News· 2 days agoCollectively, about 350 million people worldwide suffer from rare diseases, most of which are...
Gene therapy may cure rare diseasesBut drugmakers have few incentives, leaving families desperate...
The Columbian· 1 day agoRobin Alderman faces an agonizing reality: Gene therapy might cure her son Camden’s rare, inherited...
FDA expands approval of first gene therapy for rare form of muscular dystrophy
WPBF West Palm Beach· 15 hours agoThe U.S. Food and Drug Administration has given the green light for the first gene therapy that...
Decades of gene therapy research pay off big for Madison company
Wisconsin State Journal· 3 days ago“From the very start, we wanted to focus on gene therapy,” said Jim Hagstrom, a molecular biologist...
Top FDA official overrules staff to approve gene therapy that failed trial
Ars Technica· 1 day agoThe Food and Drug Administration (FDA) on Thursday announced expanded approval for a gene therapy to...
Sarepta Catapults 30% After Hitting A 'Grand Slam' Approval
Investor's Business Daily· 1 day agoThe gene therapy, dubbed Elevidys, already had accelerated approval for children age 4 and 5 with the muscle-wasting disease. Late Thursday, the Food and ...
Groundbreaking cancer treatment may trigger more cancer – but here’s why you shouldn’t worry
The Conversation· 3 days agoIn the last few decades, scientists have finally learned to harness the immune system to successfully treat cancer. Car-T therapy, short for “chimeric antigen receptor T-cell ...
Dr. Phil's staged interview with Donald Trump is a sign of the grim political theater to come
Salon via Yahoo News· 2 days agoHe rose to popularity because of his appearances on "The Oprah Winfrey Show" where he offered a...
Low-income Floridians with sickle cell disease will have access to new gene therapies
Florida Phoenix via Yahoo News· 7 days agoNow, Floridians with sickle cell disease are closer to a functional cure after health care officials...
Global Nonprofit CureDuchenne to Host Informational Webinars Following FDA Label Expansion of...
The Yuma Sun· 2 days agoThe webinars will be moderated by Dr. Michael Kelly, Chief Scientific Officer at CureDuchenne with Dr. Diana Castro, a board-certified neurologist and leading neuromuscular physician, sharing ...