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New gene delivery vehicle shows promise for human brain gene therapy
Science Daily· 5 days agoGene therapy could potentially treat a range of severe genetic brain disorders, which currently have no cures and few treatment options ...
New gene therapy model offers hope for X-linked sideroblastic anemia treatment
Medical Xpress· 7 days agoResearchers at Children's Hospital of Philadelphia have pioneered a new gene therapy model that...
How Gene Editing Therapies Could Go Beyond Rare Diseases
Forbes· 5 days agoEarlier this year, a group of scientists in the Netherlands used the gene editing tool CRISPR to...
Rae Blaylark: Legislature: Prioritize funding for sickle-cell therapy
Post-Bulletin· 1 day agoThis investment would not just signify a commitment to advancing medical innovation, but it would...
Is Bluebird Bio Stock a Buy?
Motley Fool via Yahoo Finance· 5 days agoWhat makes it the most important? ...target a maximum of 1,500 patients in the U.S. Skysona -- a therapy for a rare, progressive neurogenerative disease...
Britain slammed in inquiry for infecting thousands with tainted blood and covering up the scandal
Los Angeles Times· 19 hours agoBritish authorities and the country’s public health service knowingly exposed tens of thousands of...
Akron Children’s doctor earns distinguished national appointment
Crain's Cleveland Business· 4 days agoHord has been involved with the American Society of Pediatric Hematology/Oncology (ASPHO) throughout his career. Along with hosting an annual medical conference, ASPHO’s work centers around ...
Very rare COVID vaccine-related blood clots share genes with condition linked to common cold
FierceBiotech· 4 days agoThe rare, deadly blood clots triggered by an autoimmune response to the COVID-19 vaccines from...
Brain 'assembloids': Researchers develop first human mini-brain with fully functional blood-brain...
Medical Xpress· 20 hours agoThis major advance, published May 15 2024, in Cell Stem Cell, promises to accelerate the understanding and improve treatment of a wide range of brain disorders, including ...
Circular RNA: Vaccines, therapeutics and biomarkers could be revolutionised
Pharmaceutical Technology via Yahoo Finance· 6 days agoCircRNA is still in very early days of development, but it is expected to trialled in vaccines,...