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In a first, doctors treat fatal genetic disease before birth
Associated Press via Yahoo News· 2 years agoA toddler is thriving after doctors in the U.S. and Canada used a novel technique to treat her...
With help from Duke doctors, a rare genetic disease is treated in the womb for the first time
Raleigh News and Observer via AOL· 2 years agoFor the first time, doctors started treating a fetus with Pompe disease, a rare and often fatal...
It takes an average of 8 years for a rare disease patient to get diagnosed. Why is it so hard to get...
Fortune via Yahoo Finance· 1 year agoKey takeaways An estimated 10% of the global population suffers from rare disease; 80% of rare...
Gene therapy offers hope for rare diseases. But the stories don't always have happy endings.
USA TODAY via Yahoo News· 1 year agoNew medical treatments, such as gene therapies, have the potential to save lives or transform them...
A lifesaving therapy for children with a rare disease is now the world’s most expensive drug,...
CNN via Yahoo News· 3 months agoA new gene therapy for the fatal genetic disorder metachromatic leukodystrophy, or MLD, will carry a...
To save lives, the FDA must change how it evaluates rare disease treatments
Salon via Yahoo News· 1 month ago(Photo By Liz Hafalia/The San Francisco Chronicle via Getty Images) There are over 7,000 rare...
Dad posts heartbroken message about son’s death from a rare, treatable disease
TODAY via Yahoo News· 2 years agoNikki and Joe Monaco were devastated when their son Emmett died at age 5 of a genetic disease in...
USDA releases genetic data of bird flu after criticism from scientists
Scripps News via AOL· 2 months agoVeterinarians vaccinating farm chickens against diseases like bird flu. The U.S. Department of...
Alzheimer’s disease may be transmissible, some experts say—but only in rare, unusual circumstances....
Fortune via Yahoo Finance· 4 months agoIncredibly rare and exotic prion diseases hold uncomfortable similarities with other...
FDA approves first use of CRISPR gene editing to treat sickle cell disease
The Hill via Yahoo News· 6 months agoThe Food and Drug Administration (FDA) on Friday approved a new therapy for treating sickle cell...