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Gene therapy may cure rare diseases, drugmakers have few incentives, leaving families desperate
Warren Times Observer· 13 hours agoCamden, 21, was diagnosed as a baby with a rare disease called Wiskott-Aldrich syndrome, which is...
Alimera Sciences shares jump by 77% after being acquired by ANI
Pharmaceutical Technology via Yahoo Finance· 2 hours agoANI Pharmaceuticals is broadening its reach into the rare disease space through an acquisition of...
Generics Player ANI Pharmaceuticals Strengthens Rare Disease Segment With $380M Alimera Sciences...
Benzinga via Yahoo Finance· 2 hours agoOn Monday, ANI Pharmaceuticals Inc (NASDAQ:ANIP) agreed to acquire Alimera Sciences Inc...
Florida bills signed to target cancer and rare diseases
CBS News· 6 days agoGov. Ron DeSantis signed bills designed to help boost research into cancer and rare diseases.
Alnylam (ALNY) Stock Soars 30% on Heart Disease Drug Success
InvestorPlace· 2 hours agoHeart disease drugmaker Alnylam (NASDAQ:ALNY) stock rose sharply on the success of a Phase 3 study...
DUP manifesto: Key policies analysed
BBC via Yahoo News· 3 hours agoWhen I asked for clarity, a DUP member explained it could involve, for instance, "what they do in the south when they use independent/private healthcare...
FDA’s Sarepta decision could represent ‘new way of thinking’ for agency - Boston Business Journal
The Business Journals· 20 hours agoU.S. Food and Drug Administration’s recent decision to expand approval for a Cambridge company’s controversial gene therapy could signal a changing approach to how the federal agency deals with ...
Duchenne approval exposes FDA rift over Sarepta gene therapy
BioPharma Dive via Yahoo Finance· 3 days agoPeter Marks’ decision to override the objections of agency staff and broaden use of Elevidys could...
Celine Dion in tears as she demonstrates how rare disease affects voice
Newsweek· 5 days agoAs Celine Dion showed exactly how the rare disease she has affects her singing voice, she broke down...
Tracker Season 2: Everything We Know So Far
TV Fanatic· 3 days agoVariety reported that Tracker was the most-watched series of the 2023-2024 television season, with more than eleven million viewers tuning in each week....
