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FDA expands approval of first gene therapy for rare form of muscular dystrophy
WTAE Pittsburgh· 2 days agoThe U.S. Food and Drug Administration has given the green light for the first gene therapy that...
Sarepta’ stock soars 38% after FDA expands approval for DMD drug
Market Watch· 4 days agoThere are about 15,000 cases in the U.S., according to the Muscular Dystrophy Association. The FDA...
Children’s Hospital Los Angeles Neurology Expert | Newswise
Newswise· 5 days agoJune 20, 2024 (Los Angeles) -- Neurologist Leigh Ramos-Platt, MD, Medical Director of the Muscular Dystrophy Association Neuromuscular ...
Gene Therapy for Duchenne Muscular Dystrophy Gets Expanded Approval
MedPage Today· 4 days agoThe FDA expanded the approval of delandistrogene moxeparvovec-rokl (Elevidys) gene therapy for...
Limb girdle muscular dystrophy: Symptoms, causes, and more
Medical News Today· 6 days agoLimb-girdle muscular dystrophy (LGMD) is a group of health conditions that can cause weakness and...
Juneau revives its summer solstice spirit with Only Fools Run At Night | Juneau Empire
Juneau Empire· 3 days agoA group of rain clouds wheeling bolts of lightning in a baby stroller, a pair of ancient Incas...