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FDA expands approval of first gene therapy for rare form of muscular dystrophy
WEVV Evansville· 11 hours agoElevidys, from the biotech company Sarepta Therapeutics – was approved to treat only children ages 4 and 5 with Duchenne muscular dystrophy, one of the ...
Limb girdle muscular dystrophy: Symptoms, causes, and more
Medical News Today· 2 days agoLimb-girdle muscular dystrophy (LGMD) is a group of health conditions that can cause weakness and...
Wareham girl with muscular dystrophy treks along Jurassic coast
BBC News· 4 hours agoA 10-year-old girl with muscular dystrophy is travelling 100 miles over two weeks to raise money for charity. Carmela, from Wareham, began walking, and ...
Sarepta Skyrockets After Nabbing A Broad Label For Its Duchenne Gene Therapy
Investor's Business Daily· 9 hours agoSarepta stock rocketed late Thursday after the Food and Drug Administration approved its Duchenne ...
Sarepta jumps on broad approval for muscular dystrophy drug - The Boston Globe
The Boston Globe· 9 hours agoSarepta shares surged 36% in extended trading at 5:51 p.m. in New York. The drug’s approval was...
Sarepta Therapeutics surges 36% after-hours following expanded FDA approval By Investing.com
Investing.com· 11 hours agoThe drug can now be used for patients aged 4 and above who have Duchenne muscular dystrophy (DMD), a...
Global Nonprofit CureDuchenne to Host Informational Webinars Following FDA Label Expansion of...
FOX 23 News Albany· 9 hours agoCureDuchenne, a global nonprofit committed to finding and funding a cure for Duchenne muscular dystrophy, will host webinars in English and Spanish for ...
Children’s Hospital Los Angeles Neurology Expert | Newswise
Newswise· 1 day agoJune 20, 2024 (Los Angeles) -- Neurologist Leigh Ramos-Platt, MD, Medical Director of the Muscular Dystrophy Association Neuromuscular Clinic at Children ...
US FDA approves expanded use of Sarepta's Duchenne gene therapy
Reuters· 11 hours ago, opens new tab gene therapy for all patients with Duchenne muscular dystrophy aged four and above...
These Stocks Are Moving the Most Today: Microsoft, Nvidia, Trump Media, Sarepta, CarMax, and More
Barrons.com· 14 minutes agoMicrosoft again tops Nvidia as the world’s most valuable company, Trump Media shares post a modest...