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    • Neuren Phase 2 trial shows significant improvements in Pitt Hopkins syndrome

      FOX21 Colorado Springs· 5 hours ago

      ...baseline assessed by both clinicians and caregivers in all four efficacy measures specifically designed for Pitt Hopkins syndrome (Wilcoxon signed rank test p<0.05)Clinician and caregiver global efficacy measures showed a level of improvement considered clinically meaningful:- Clinical Global...