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Amgen’s drug meets main goal in late-stage study for rare disease
KFGO· 5 days ago(Reuters) - Amgen said on Wednesday its drug to treat patients with an immune system-related...
Celine Dion Describes Horror of Singing With Stiff-Person Syndrome
The Daily Beast via Yahoo News· 3 days agoShe first revealed to the world that she was diagnosed with Stiff-Person Syndrome...
Rare disease's DNA-damaging mutation could have consequences for more common conditions
Science Daily· 6 days ago"It seems that accelerated DNA damage in RVCL causes the premature aging of certain cells, including the cells in the blood vessel wall," said the study's lead author Jonathan Miner, MD, PhD ...
Denali, Neurogene and more picked by FDA's 'Operation Warp Speed' for rare disease
FierceBiotech· 5 days agoThe FDA’s “Operation Warp Speed” equivalent for rare disease will include programs from Denali...
After key rare disease win, Annexon eyes $144 million raise - San Francisco Business Times
The Business Journals· 5 days agoAnnexon Inc. hopes to sell $125 million of stock following a late-stage clinical trial of a drug...
Amgen's drug meets main goal in late-stage study for rare disease
Reuters via AOL· 5 days ago(Reuters) -Amgen said on Wednesday its drug helped to reduce the risk of flares in patients with an...
Annexon’s neurological disease drug meets main goal of late-stage study
WSAU Wausau· 6 days ago(Reuters) -Annexon said on Tuesday its experimental drug to treat a rare neurological disease met the main goal of a late-stage trial, sending its shares ...
Charlotte, the pregnant stingray with no male partner, has a 'rare reproductive disease'
Scripps News via AOL· 6 days agoA female stingray who gained national attention after she became pregnant despite not having a male...
Moderna mRNA candidate chosen for FDA rare disease therapy acceleration program
Seeking Alpha· 4 days agoThe FDA selects Moderna's mRNA therapeutic mRNA-3705 for a pilot program to accelerate development...
...AI’s Pentavere Announces Partnership with Takeda to Support Rare Disease Real-World Evidence...
Digital Journal· 4 days ago(“Takeda”) to drive real-world evidence analysis for rare diseases, particularly focusing on supporting patients suffering from hereditary angioedema (HAE ...