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Gene therapy may cure rare diseases, drugmakers have few incentives, leaving families desperate
Warren Times Observer· 6 hours agoCamden, 21, was diagnosed as a baby with a rare disease called Wiskott-Aldrich syndrome, which is...
Duchenne approval exposes FDA rift over Sarepta gene therapy
BioPharma Dive via Yahoo Finance· 3 days agoPeter Marks’ decision to override the objections of agency staff and broaden use of Elevidys could...
Elon Musk & Shivon Zilis Welcome Their Third Baby Together
E! News via Yahoo News· 13 hours ago"I brought my children up like my parents brought us up when we were young: to be independent, kind,...
Decades of gene therapy research pay off big for Madison company
Wisconsin State Journal· 4 days agoThirty years ago, when the idea that would give rise to Mirus Bio took shape in a UW-Madison...
Country music world hit hard by another death in tragic year
The Patriot-News· 55 minutes agoIt has been a heartbreaking year for the country music world as the list of legendary performers and...
Foundation Honoring 'Star Trek' Creator Offers $1M Prize for AI Startup Benefiting Humanity -...
Slashdot· 17 hours agoThe Roddenberry Foundation — named for Star Trek creator Gene Roddenberry — "announced Tuesday that this year's biennial award would focus on artificial intelligence that ...
Businesses are rushing to use generative AI. Now comes the messy part.
Business Insider via Yahoo News· 5 days agoGene Rapoport, who leads Generative AI initiatives for Bain...revenue is one, but costs coming down...
US FDA approves expanded use of Sarepta's Duchenne gene therapy; shares jump
Reuters via AOL· 4 days ago(Reuters) -The U.S. Food and Drug Administration allowed the expanded use of Sarepta Therapeutics' ...
In drug-pricing debate, Mass. gene-therapy drugmakers make their case - Boston Business Journal
The Business Journals· 3 days agoWhen a new gene therapy to treat a deadly rare disease called metachromatic leukodystrophy was approved earlier this year, the first thing on Maria Kefalas’ mind wasn’t the ...
Sarepta stock soars on Duchenne gene therapy expanded approval - Boston Business Journal
The Business Journals· 3 days agoShares of Sarepta Therapeutics shot up nearly 35% when markets opened Friday, following the FDA's...