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Duchenne approval exposes FDA rift over Sarepta gene therapy
BioPharma Dive via Yahoo Finance· 2 days agoPeter Marks’ decision to override the objections of agency staff and broaden use of Elevidys could...
Gene therapy may cure rare diseases. But drugmakers have few incentives, leaving families desperate...
Chattanooga Times Free Press· 2 days agoRobin Alderman faces an agonizing reality: Gene therapy might cure her son Camden's rare, inherited immune deficiency. In 2022, London-based Orchard Therapeutics stopped investing ...
Foundation Honoring 'Star Trek' Creator Offers $1M Prize for AI Startup Benefiting Humanity -...
Slashdot· 4 hours agoThe Roddenberry Foundation — named for Star Trek creator Gene Roddenberry — "announced Tuesday that this year's biennial award would focus on artificial intelligence that ...
Research paying off for Madison company
Wisconsin State Journal· 13 hours agoThirty years ago, when the idea that would give rise to Mirus Bio took shape in a UW-Madison laboratory, scientists were only beginning to piece together...
Businesses are rushing to use generative AI. Now comes the messy part.
Business Insider via Yahoo News· 4 days agoGene Rapoport, who leads Generative AI initiatives for Bain...revenue is one, but costs coming down...
US FDA approves expanded use of Sarepta's Duchenne gene therapy; shares jump
Reuters via AOL· 3 days ago(Reuters) -The U.S. Food and Drug Administration allowed the expanded use of Sarepta Therapeutics' ...
Sarepta stock soars on Duchenne gene therapy expanded approval - Boston Business Journal
The Business Journals· 2 days agoShares of Sarepta Therapeutics shot up nearly 35% when markets opened Friday, following the FDA's...
In drug-pricing debate, Mass. gene-therapy drugmakers make their case - Boston Business Journal
The Business Journals· 3 days agoWhen a new gene therapy to treat a deadly rare disease called metachromatic leukodystrophy was approved earlier this year, the first thing on Maria Kefalas’ mind wasn’t the ...
3 Reasons Self-Made Millionaires Who Didn’t Get a Prenup Might Regret it and 1 Reason Why They Might...
GOBankingRates via Yahoo Finance· 8 hours agoThere are several misconceptions about having a prenuptial agreement, such as the idea that it is...
Sarepta Stock Surges on Expanded Elevidys Approval. It’s a ‘Best-Case’ Scenario for Shares.
Barrons.com· 2 days agoThe biopharmaceutical company says the drug was approved for ambulatory and non-ambulatory people,...