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The FDA is failing children with a rare, neglected disease sometimes called "childhood dementia"
Salon via Yahoo News· 5 months agoSad little boy at home Getty Images/kieferpix The effects of Sanfilippo syndrome in small children...
Family of a Muskego 3-year-old with a terminal illness is raising $1 million for a chance to save...
Milwaukee Journal Sentinel via Yahoo News· 1 year agoWhen 3-year-old Olivia (Liv) Stoop of Muskego was very little, she was "obsessed" with her baby...
For Palm Coast mom, a TikTok video led to diagnosis of daughter's rare disease
Daytona Beach News-Journal via Yahoo News· 2 months agoPALM COAST — As the U.S. House of Representatives passed a bill earlier this month that could result...
What she does for love: Caring for her son who is losing his ability to walk and talk
Miami Herald via Yahoo News· 6 months agoKenia Cutie moved to Miami in 2011 with dreams of strolling down the Miami shoreline with her son...
To save lives, the FDA must change how it evaluates rare disease treatments
Salon via Yahoo News· 1 month ago(Photo By Liz Hafalia/The San Francisco Chronicle via Getty Images) There are over 7,000 rare...
Jordan Love sent a personalized football to 4-year-old girl in Muskego who has a rare fatal genetic...
Milwaukee Journal Sentinel via Yahoo Sports· 4 months agoMuskego 4-year-old Olivia "Liv" Stoop, who has a rare fatal genetic disorder, received a rare gift...
All-star roster of 14 national & local chefs cooking together in support of one of their own
Delaware Online | The News Journal via Yahoo News· 1 year agoIt's pretty rare to have nearly 15 of some of the best-known chefs in Delaware all cooking and...
North Carolina girl with ‘childhood dementia’ becomes social media star
WJZY via Yahoo News· 3 months agoSTANLY COUNTY, N.C. (WGHP) — As a second grader, Sadie Haywood has managed to build something many...
Ultragenyx Pharmaceutical Inc. (NASDAQ:RARE) Q4 2022 Earnings Call Transcript
Insider Monkey via Yahoo Finance· 1 year agoUltragenyx Pharmaceutical Inc. (NASDAQ:RARE) Q4 2022 Earnings Call Transcript February 16, 2023...
Ultragenyx's (RARE) Q2 Earnings Miss Estimates, Revenues Up
Zacks via Yahoo Finance· 2 years agoUltragenyx Pharmaceutical Inc. RARE incurred a loss of $2.26 per share in second-quarter 2022, wider...