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Vertex says Casgevy benefit extends to nearly five years in sickle cell disease
Clinical Trials Arena via Yahoo Finance· 1 hour agoVertex Pharmaceuticals has reported long-term data for its gene therapy Casgevy (exa-cel) in...
You Can Help People Living with Sickle Cell Disease
St. Louis Post-Dispatch· 4 days ago“I love using my voice for the people who are not heard and showing the world what you can do, even with a disability,” said Green, who was diagnosed...
IV infusion enables editing of the cystic fibrosis gene in lung stem cells
Ars Technica· 18 hours agoThe development of gene editing tools, which enable the specific targeting and correction of...
Shining a light on World Sickle Cell Awareness Day. Learn more about this rare blood disorder
Delaware Online | The News Journal via Yahoo News· 3 days agoAround 100,000 people in the U. S. — including an estimated 600 to 700 people in Delaware — and...
World Sickle Cell Day 2024
Digital Journal· 3 days agoSickle Cell Day 2024 event aims to unite participants worldwide, emphasizing the global significance of this genetic blood disorder. "Our World
Blood matching tests by the NHS may improve blood transfusion outcomes
Clinical Trials Arena via Yahoo Finance· 2 days agoAccording to the National Institute for Health and Care Excellence (NICE), sickle cell disease, a...
New hope for those living with Sickle Cell Disorder thanks to experimental gene treatment
WSB-TV 2 Atlanta· 6 days agoThe treatment is a gene cell therapy recently approved by the U.S. Food and Drug Administration. For...
A rural Ugandan community is a hot spot for sickle cell disease. But one patient gives hope
McComb Enterprise-Journal· 5 days agoBarbara Nabulo cleans clothes at her home in Busamaga-Mutukula village in Mbale, Uganda, Thursday, April 25, 2024. There can be lifelong challenges for people with sickle ...
Phelps Hospital holds Inaugural World Sickle Cell Day event
News 12· 1 day agoPhelps Hospital held an inaugural World Sickle Cell Day event on Wednesday to raise awareness about the disease. The awareness day is ...
The Cream Of The Crop: 5 Biotechs That Outrank Most Stocks
Investor's Business Daily· 20 hours agoVertex and partner Crispr Therapeutics gained Food and Drug Administration approval for a...