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FDA expands approval of first gene therapy for rare form of muscular dystrophy
CNN.com· 10 hours agoThe US Food and Drug Administration has given the green light for the first gene therapy that treats...
Gene therapy may cure rare diseases. But drugmakers have few incentives, leaving families desperate
Associated Press via Yahoo News· 22 hours agoRobin Alderman faces an agonizing reality: Gene therapy might cure her son Camden’s rare, inherited...
Sarepta Catapults 30% After Hitting A 'Grand Slam' Approval In Muscular Dystrophy
Investor's Business Daily· 6 hours agoSarepta stock rocketed Friday after hitting a "grand slam" approval that expands the market for its...
Sarepta surges as investors cheer expanded use of gene therapy
Reuters via Yahoo News· 16 hours ago(Reuters) -Sarepta Therapeutics shares surged as much as 40% to a more than three-year high on Friday as an expanded use approval cemented its dominant position in the gene
Sarepta Gains as FDA Official Overrules Staff to Approve Therapy
Bloomberg via Yahoo Finance· 12 hours ago(Bloomberg) -- A top US Food and Drug Administration official overrode reviewers to give broad...
Sarepta Skyrockets After FDA Signs Off On Duchenne Gene Therapy
Investor's Business Daily· 16 hours agoLast year, the FDA granted the Sarepta Therapeutics (SRPT) gene therapy, dubbed Elevidys, an accelerated approval for children ages 4 and 5 with Duchenne ...
US FDA approves expanded use of Sarepta’s Duchenne gene therapy
WHTC 1450 Holland· 1 day ago(Reuters) -The U.S. Food and Drug Administration allowed the expanded use of Sarepta Therapeutics' ...
Taysha links gene therapy to motor gains in small Rett study
FierceBiotech· 3 days agoTaysha Gene Therapies has unfurled more data in the developmental disorder Rett syndrome, linking...
Sarepta Duchenne gene therapy wins broader use from FDA
BioPharma Dive via Yahoo Finance· 1 day agoThe approval makes Elevidys available to most Duchenne patients at least 4 years of age, despite...
Decades of gene therapy research pay off big for Madison company
Wisconsin State Journal· 1 day ago“From the very start, we wanted to focus on gene therapy,” said Jim Hagstrom, a molecular biologist...