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What happens when a $2 million gene therapy is not enough
Reuters via Yahoo News· 10 months agoBaby Ben Kutschke was diagnosed at three months with spinal muscular atrophy, a rare inherited...
The Most Expensive Drug From Novartis Associated With Two Deaths: Report
Benzinga via Yahoo Finance· 2 years agoTwo children with spinal muscular atrophy have died after receiving Novartis AG's (NYSE: NVS)...
Novartis reports Zolgensma caused two deaths from liver failure
Reuters via Yahoo News· 2 years agoThe company has notified health authorities in markets where the drug is sold, including the FDA,...
Most babies with this rare genetic disease are on ventilators by 8 months. This Austin baby beat the...
Austin American-Statesman via Yahoo News· 2 years agoNoah Strauch loves to laugh. He loves to put things into a bucket and dump them out again. He crawls...
Novartis (NVS) Q2 Earnings Beat, Revenues Miss Estimates
Zacks via Yahoo Finance· 2 years agoNovartis AG NVS reported mixed second-quarter 2022 results. The Sandoz business continues to recover...
Regenxbio CEO to step down after 15 years
BioPharma Dive via Yahoo Finance· 7 hours agoKenneth Mills will become chair of the gene therapy developer's board while Curran Simpson, the current chief operating officer, will take his place as...
Roche's (RHHBY) Evrysdi Gets Label Expansion in EU for Newborns
Zacks via Yahoo Finance· 9 months agoRoche RHHBY announced that the European Commission (“EC”) had approved the label expansion for...
Twin 'was just melting': Babies with neuromuscular disease find new hope in Austin
Austin American-Statesman via Yahoo News· 2 years agoJenny and Jarod Carter's twins weren't making their typical infant milestones after they were born...
Novartis (NVS) Q2 2022 Earnings Call Transcript
Motley Fool· 2 years agoImage source: The Motley Fool. Novartis (NYSE: NVS) Q2 2022 Earnings Call Jul 19, 2022, 8:00 a.m. ET Contents: Prepared Remarks Questions and Answers...
Regenxbio Inc (RGNX) Reports Full Year 2023 Financial Results and Operational Highlights
GuruFocus.com via Yahoo Finance· 3 months agoCash Position: $314.1 million as of December 31, 2023, funding operations into H2 2025. Revenues:...