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Kate Therapeutics Unveils Platform and Pipeline Progress at American Society of Gene & Cell Therapy...
FOX21 Colorado Springs· 6 hours agoThe results support the best-in-class potential of KateTx's newest generation of skeletal muscle- and heart-targeted, liver de-targeted engineered MyoAAV capsids and gene regulation technology ...
Regenex Bio eyes FDA meeting to confirm pivotal DMD trial
Clinical Trials Arena via Yahoo Finance· 5 hours agoRegenex Bio has announced it is meeting with the US Food and Drug Administration (FDA) with plans to...
How Top 7% Earnings Powerhouse Catalyst Pharmaceuticals Just Did It Again
Investor's Business Daily· 2 hours agoIn response, the biotech stock jumped Thursday. Agamree treats a muscle-wasting disease known as...
Second Death - Pfizer Reports Young Boy's Death After One Year Of Gene Therapy Treatment In Muscle...
Benzinga via Yahoo Finance· 21 hours agoA young patient died due to cardiac arrest after receiving Pfizer Inc’s (NYSE:PFE) experimental gene...
Young Patient Dies After Receiving Pfizer Gene Therapy
Futurism via Yahoo News· 3 hours agoTragedy has struck during an important Pfizer medical trial when a young boy suffered a fatal sudden...
Pfizer pauses phase 3 dosing in gene therapy trial after young boy's death
FierceBiotech· 2 days agoA young boy with Duchenne muscular dystrophy (DMD) participating in Pfizer’s phase 2 gene therapy...
Mom urges state to add Duchenne muscular dystrophy to newborn screening panel
WTHR Indianapolis· 6 days agoDuchenne muscular dystrophy affects at least 1 in 5,000 male births each year, and girls can be...
Child dies in gene therapy trial; Pfizer pauses study
Becker’s Hospital Review· 1 day agoA boy has died in Pfizer's phase 2 study of its gene therapy candidate for Duchenne muscular dystrophy, a rare genetic disorder that primarily affects boys ...
Firefighters gear up for MDA's Fill the Boot fundraiser
The Eastsider· 2 days agoThe Muscular Dystrophy Association (MDA) is spreading awareness and funds through its annual Fill...
Gypsy Rose Blanchard Finds 'Beauty' in 'the Struggle of Overcoming' Her Past as She Shares Photos of...
OK! Magazine· 1 day agoFrom a victim of abuse to a prisoner and now a pop-culture phenomenon, Gypsy Rose Blanchard has been...