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“Celebrity Wheel of Fortune” contestant Christian Siriano also designed Vanna White's dress
Entertainment Weekly via Yahoo News· 13 hours agoMeanwhile, Schitt's Creek alum Levy is competing for FSHD Society, a research-focused patient...
Gypsy Rose Blanchard returns to TikTok after her apology for 'lack of accountability' following...
The Today Show via AOL· 4 days agoOn the stand, Gypsy Rose Blanchard described how her mother took her to doctors throughout her life...
Mom urges state to add Duchenne muscular dystrophy to newborn screening panel
WTHR Indianapolis· 4 days agoDuchenne muscular dystrophy affects at least 1 in 5,000 male births each year, and girls can be...
Sarepta Elevidys accelerated approval criticized by ICER exec
Seeking Alpha· 4 days agoFDA's accelerated approval drug process is under fire from a prominent medical expert who called out...
Investigational FSHD Drug Did Little to Change DUX4 Expression
MedPage Today· 5 days agoThe investigational drug losmapimod did not significantly change expression of the gene behind...
Robotic Arm Provides Independence
The Harrisonburg Daily News-Record· 5 days agoThings 23-year-old Wade Custer thought were unthinkable are now possible. Wade, from Mount Jackson, was diagnosed with Duchenne Muscular Dystrophy at an...
1 Top Growth Stock to Buy and Hold for 10 Years
Motley Fool via Yahoo Finance· 6 days agoFood and Drug Administration (FDA). But first, some background information. Sarepta develops therapies for rare diseases. Its most important area of...
The FDA and Gene Therapy for Duchenne Muscular Dystrophy
Journal of the American Medical Association· 6 days agoThe US Food and Drug Administration (FDA) grants accelerated approval that includes the standard of a surrogate outcome that is “reasonably likely” to predict clinical benefit.1 Gene therapy ...
Local firefighters to participate in annual Fill the Boot campaign for Muscular Dystrophy...
Arizona Daily Sun· 7 days agoThe International Association of Fire Fighters (IAFF) has collected funds in communities since 1954...
TIME100 Health: Jerry Mendell
Time via Yahoo News· 5 days agoJerry Mendell Credit - Courtesy Nationwide Children’s Hospital In the 1960s, Dr. Jerry Mendell saw his first patient with Duchennemuscular dystrophy....
