Search results
Kate Therapeutics Unveils Platform and Pipeline Progress at American Society of Gene & Cell Therapy...
FOX21 Colorado Springs· 13 hours agoThe results support the best-in-class potential of KateTx's newest generation of skeletal muscle- and heart-targeted, liver de-targeted engineered MyoAAV capsids and gene regulation technology ...
Second Death - Pfizer Reports Young Boy's Death After One Year Of Gene Therapy Treatment In Muscle...
Benzinga via Yahoo Finance· 1 day agoA young patient died due to cardiac arrest after receiving Pfizer Inc’s (NYSE:PFE) experimental gene...
How Top 7% Earnings Powerhouse Catalyst Pharmaceuticals Just Did It Again
Investor's Business Daily· 3 hours agoIn response, the biotech stock jumped Thursday. Agamree treats a muscle-wasting disease known as...
Young Patient Dies After Receiving Pfizer Gene Therapy
Futurism via Yahoo News· 10 hours agoTragedy has struck during an important Pfizer medical trial when a young boy suffered a fatal sudden...
Regenex Bio eyes FDA meeting to confirm pivotal DMD trial
Clinical Trials Arena via Yahoo Finance· 12 hours agoRegenex Bio has announced it is meeting with the US Food and Drug Administration (FDA) with plans to...
Mom urges state to add Duchenne muscular dystrophy to newborn screening panel
WTHR Indianapolis· 7 days agoDuchenne muscular dystrophy affects at least 1 in 5,000 male births each year, and girls can be...
Pfizer pauses phase 3 dosing in gene therapy trial after young boy's death
FierceBiotech· 2 days agoA young boy with Duchenne muscular dystrophy (DMD) participating in Pfizer’s phase 2 gene therapy...
These congressmen want to modify the Inflation Reduction Act to foster rare disease research
The Hill via Yahoo News· 2 hours agoReps. John Joyce (R-Pa.) and Wiley Nickel (D-N.C.) on Thursday discussed why they’re pushing to pass...
Firefighters gear up for MDA's Fill the Boot fundraiser
The Eastsider· 2 days agoThe Muscular Dystrophy Association (MDA) is spreading awareness and funds through its annual Fill...
“Celebrity Wheel of Fortune” contestant Christian Siriano also designed Vanna White's dress
Entertainment Weekly via Yahoo News· 3 days agoMeanwhile, Schitt's Creek alum Levy is competing for FSHD Society, a research-focused patient...