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Potential Effects of the Inflation Reduction Act on Orphan Drug Development | JD Supra
JD Supra· 4 days agoDuring the notice and comment period leading up to the implementation of the IRA, the Centers for Medicare & Medicaid Services (CMS) maintained that “a drug that has orphan designations ...
Remix Therapeutics Announces First Patients Dosed in Two Phase 1 Clinical Trials Investigating...
WFRV 5 Green Bay· 3 days agoAdditionally, the company also announced that REM-422 has received Orphan Drug Designation from the FDA for the treatment of ACC and ...
Napo Pharmaceuticals, a Jaguar Health Family Company, Sponsoring Pediatric Gastroenterology...
Digital Journal· 6 days agoJaguar's novel plant-based prescription drug crofelemer has been granted Orphan Drug Designation by the FDA and the European Medicines ...
Poolbeg Pharma agrees 12 month option over orphan drug with fast-track potential
Proactive Investors· 5 days ago(AIM:POLB, OTCQB:POLBF) has inked an exclusive 12-month option agreement to acquire a phase...
Poolbeg Pharma PLC Announces Option Agreement to Acquire Orphan Drug Candidate
Digital Journal· 5 days agoLONDON, UK / ACCESSWIRE / April 30, 2024 / Poolbeg Pharma (AIM:POLB)(OTCQB:POLBF), 'Poolbeg' or the 'Company'), a biopharmaceutical company focussed on the development and commercialisation ...
Remix Therapeutics doses first subjects in Phase I cancer treatment trials
Clinical Trials Arena via Yahoo Finance· 2 days agoIn addition to the trial commencement, Remix announced that REM-422 received orphan drug designation...
FDA grants breakthrough status to Soleno's PWS drug By Investing.com
Investing.com· 6 days agoSoleno Therapeutics, Inc. (NASDAQ: NASDAQ:SLNO) has received Breakthrough Therapy Designation from...
Soleno Therapeutics Shares Rise 37% After Breakthrough Designation for Diazoxide Choline
Market Watch· 6 days agoBy Chris Wack Soleno Therapeutics were trading near a three-year high after the Food and Drug Administration granted breakthrough therapy designation for...
These 2 ‘Strong Buy’ Penny Stocks Could Rally to $9, Says Piper Sandler
TipRanks via Yahoo Finance· 6 days ago‘Audentes Fortuna iuvat,’ wrote Virgil in his classic epic, the Aeneid. The saying, translated as...
Prime Medicine gets green light for trials of first-ever prime editing drug
Clinical Trials Arena via Yahoo Finance· 5 days agoThe drug comprises autologous blood stem cells modified ex vivo using prime editing to correct a...